Prophylactic cardiac treatment may prolong survival in Duchenne muscular dystrophy (DMD), but only one-quarter of individuals ...
Children's Mercy Kansas City has achieved a significant advancement toward the treatment of rare genetic diseases through the ...
As a parent and caregiver to three sons with DMD, columnist Betty Vertin's definition of what success looks like has changed over the years.
The Shanghai-based firm will test the gene therapy candidate in patients between 4 and 9 years old with Duchenne muscular dystrophy.
The US Food and Drug Administration (FDA) has granted Rare Pediatric Disease (RPD) designation to NS-051/NCNP-04, which is ...
Despite mixed results using gene therapies to treat Duchenne muscular dystrophy, drug developers are pushing ahead with the ...
The West Texas Rehab Telethon will be taking place this weekend. This event is to give back to people and facilities that care for people in need.
Governor Maura Healey’s budget proposal includes major cuts to health and social service programs, including two residential ...
Learn about the world’s most expensive watches, from Jackie Kennedy’s Cartier to Paul Newman’s Rolex Daytona. Which one tops $31M?
One of the most anticipated and noteworthy wine events of the year, Napa in Newport, returns to the Pendry in Fashion Island on March 1, and it promises to be another stellar evening of superb wines ...
According to Dr Ann Agnes Mathew, Consultant Pediatric Neurologist at Bangalore Baptist Hospital, DMD is life-threatening and ...
A new study published in the peer-reviewed journal Muscle & Nerve shows that full-spectrum cannabidiol (CBD) oil may help ...