Based on a small trial with positive muscle performance data, Regenxbio is expected to pursue approval of its gene therapy ...

Myotonic dystrophy is an inherited muscular dystrophy causing muscle weakness and wasting. Excessive daytime sleepiness (hypersomnia) is a frequent complaint of people with myotonic dystrophy and is ...

StitchR makes it possible to deliver larger payloads with current vectors, expanding the list of diseases targetable by gene therapies.

StitchR, a new gene therapy technique, delivers large genes in two parts to treat muscular dystrophies by restoring critical proteins in animal models.

Gene therapy can effectively treat various diseases, but for some debilitating conditions like muscular dystrophies there is ...

Pratteln, Switzerland, November 12, 2024 – Santhera Pharmaceuticals (SIX: SANN) announces the signing of an exclusive supply agreement with Ali Al Suwaidi Trading Est. (ASTE) for the treatment of ...

First patient dosed in Phase 1/Phase 2 LION-CS101 trial of AB-1003 in August 2023, with enrollment continuing Asklepios BioPharmaceutical, Inc. (AskBio), a gene therapy company wholly owned and ...

Print your poster on campus. For best results, print your research poster through University Print Services. This is UB's preferred, on-campus vendor with lower costs than outside vendors and an ...

Also there for the celebration: Former Southeast High School Principal Brent Toalson and his 29-year-old son Alex, who has Duchenne muscular dystrophy, a progressive genetic disease where abnormal ...

Cynthia Erivo explained why she felt so passionately about a fan-edited “Wicked” poster after receiving backlash over her response. When asked about the viral moment at the CFDA Fashion ...

While speaking with Entertainment Tonight on the red carpet at the 2024 CFDA Fashion Awards on Monday, the actress, 37, admitted blasting the poster on social media earlier this month was a “human ...

That is why the Tony Award winner—who portrays Elphaba in the film alongside Ariana Grande’s Glinda the Good Witch—didn’t hold back when she recently criticized an edit of the movie poster ...