Have you or your child recently been diagnosed with MPS or ML, or is your child undergoing diagnostic testing? We are here to help and can connect you with the information you need. …

Their engineered cell therapies are designed to restore cell function in patients living with chronic diseases such as lysosomal diseases and other rare disorders. They are expecting to initiate …

MPS II is a mucopolysaccharide disease known as Hunter syndrome. It takes its name from Charles Hunter, the professor of medicine in Manitoba, Canada, who first described two …

MPS I (Hurler-Scheie syndrome ) is caused by a recessive gene. There is a one in four chance with every pregnancy that the child will inherit the defective gene from each carrier parent and …

MPS diseases end up affecting nearly every part of the body, damaging the heart, bones, joints, respiratory system and central nervous system. All MPS diseases are terminal.

With an initial focus on MPS II, we are launching the 100 Patient Project to harness the revolutionary insights that can come from Whole Genome Sequencing (WGS) to better …

Learn more about the rare diseases the National MPS Society is fighting to cure, including MI, Sanfilippo, Hunter, and Hurler syndromes.

Es gibt keine Heilung für MPS oder Myokardinfarkt, aber die Forschung entdeckt immer wieder Behandlungsmöglichkeiten, um die Lebensqualität der Betroffenen zu verbessern.

Through BPPS, patients receive live, personalized support by a specialized case manager who will research insurance coverage and alternative benefit options. BPPS will help patients …

MPS IV, or Morquio syndrome, is one of the rarest MPS diseases in the US. Learn more about MPS IV symptoms and treatments.